@article{UBHD-68703981, author={B{\"o}rner, Kathleen and Kienle, Eike and Huang, Lin-Ya and Weinmann, Jonas and Sacher, Anna and Bayer, Philipp and St{\"u}llein, Christian and Fakhiri, Julia and Zimmermann, Laura and Westhaus, Adrian and Beneke, J{\"u}rgen and Beil, Nina and Wiedtke, Ellen and Schmelas, Carolin and Miltner, Dominik and Rau, Alexander and Erfle, Holger and Kr{\"a}usslich, Hans-Georg and M{\"u}ller, Martin and Agbandje-McKenna, Mavis and Grimm, Dirk}, title={Pre-arrayed Pan-AAV peptide display libraries for rapid single-round screening}, year={2020}, pages={1016-1032}, language={eng}, issn={1525-0024}, volume={28}, number={4}, note={Gesehen am 25.02.2021}, journal={Molecular therapy}, doi={10.1016/j.ymthe.2020.02.009}, } @article{UBHD-68334927, author={Bubeck, Felix and Hoffmann, Mareike and Bietz, Andreas and Waldhauer, Max and B{\"o}rner, Kathleen and Fakhiri, Julia and Schmelas, Carolin and Dietz, Laura and Grimm, Dirk and Eils, Roland and Niopek, Dominik}, title={Engineered anti-CRISPR proteins for optogenetic control of CRISPR-Cas9}, year={2018}, pages={924-927}, language={eng}, issn={1548-7105}, volume={15}, number={11}, note={Das PDF enth{\"a}lt 4 Seiten Text und 6 Seiten Anhang ; Gesehen am 03.12.2018}, journal={Nature methods}, doi={10.1038/s41592-018-0178-9}, } @article{UBHD-68892230, author={Fakhiri, Julia and Landegger, Lukas and Grimm, Dirk}, title={Breaking the sound barrier}, subtitle={towards next-generation AAV vectors for gene therapy of hearing disorders}, year={2022}, pages={1-16}, language={eng}, issn={1878-5891}, volume={413}, number={Artikel-ID 108092}, note={Vorab ver{\"o}ffentlich 2020 ; Gesehen am 07.03.2022}, journal={Hearing research}, doi={10.1016/j.heares.2020.108092}, } @article{UBHD-68628834, author={Fakhiri, Julia and Linse, Kai-Philipp and Schneider, Marc and Meister, Michael and Schnitzler, Paul and Grimm, Dirk}, title={Impact of natural or synthetic singletons in the capsid of human bocavirus 1 on particle infectivity and immunoreactivity}, year={2020}, pages={1-23}, language={eng}, issn={1098-5514}, volume={94}, note={Gesehen am 19.08.2020}, journal={Journal of virology}, doi={10.1128/JVI.00170-20}, } @article{UBHD-68380404, author={Fakhiri, Julia and Schneider, Marc and Stanifer, Megan and Holderbach, Stefan and Voss, Yannik and El Andari, Jihad and Boulant, Steeve and Meister, Michael and Grimm, Dirk}, title={Novel chimeric gene therapy vectors based on adeno-associated virus and four different Mammalian bocaviruses}, year={2019}, pages={202-222}, language={eng}, issn={2329-0501}, volume={12}, note={Available online 18 January 2019 ; Gesehen am 15.04.2019}, journal={Molecular therapy}, doi={10.1016/j.omtm.2019.01.003}, } @incollection{UBHD-68583344, author={Fakhiri, Julia and Nickl, Manuela and Grimm, Dirk}, title={Rapid and simple screening of CRISPR guide RNAs (gRNAs) in cultured cells using adeno-associated viral (AAV) vectors}, year={2019}, pages={111-126}, language={eng}, isbn={978-1-4939-9170-9}, note={Gesehen am 03.06.2020}, booktitle={CRISPR gene editing}, editor={Luo, Yonglun}, doi={10.1007/978-1-4939-9170-9_8}, } @book{UBHD-68452960, author={Fakhiri, Julia}, title={With small viruses come giant responsibilities}, subtitle={next-generation parvoviral vectors for human gene therapy with extended packaging capacity and enhanced safety profile}, address={Heidelberg}, year={2019}, pages={1 Online-Ressource (197 Seiten)}, language={eng}, school={Dissertation, Ruperto-Carola University Heidelberg, 2019}, doi={10.11588/heidok.00027326}, keywords={Parvoviren / Dependoviren / Gentherapie / Humanes Bocavirus}, url={https://nbn-resolving.org/urn:nbn:de:bsz:16-heidok-273265}, library={UB}, } @book{UBHD-68468780, author={Fakhiri, Julia}, organization={Universit{\"a}t Heidelberg}, title={With small viruses come giant responsibilities}, subtitle={next-generation parvoviral vectors for human gene therapy with extended packaging capacity and enhanced safety profile}, address={Heidelberg}, year={2019}, pages={197 Seiten}, language={eng}, school={Dissertation, Ruperto-Carola University Heidelberg, 2019}, keywords={Parvoviren / Dependoviren / Gentherapie / Humanes Bocavirus}, library={UB [Signatur: 2019 U 1024]}, } @article{UBHD-68259162, author={Große, Stefanie and B{\"o}rner, Kathleen and Fakhiri, Julia and Laketa, Vibor and Wiedtke, Ellen and Gunkel, Manuel and Grimm, Dirk}, title={Relevance of assembly-activating protein for adeno-associated virus vector production and capsid protein stability in mammalian and insect cells}, year={2017}, pages={20 S.}, language={eng}, issn={1098-5514}, volume={91(2017}, note={Posted online 2 August 2017 ; Gesehen am 08.06.2018}, journal={Journal of virology}, doi={10.1128/JVI.01198-17}, } @article{UBHD-68470832, author={Hoffmann, Mareike and Aschenbrenner, Sabine and Große, Stefanie and Rapti, Kleopatra and Domenger, Claire and Fakhiri, Julia and Mastel, Manuel and B{\"o}rner, Kathleen and Eils, Roland and Grimm, Dirk and Niopek, Dominik}, title={Cell-specific CRISPR-Cas9 activation by microRNA-dependent expression of anti-CRISPR proteins}, year={2019}, pages={15 S.}, language={eng}, issn={1362-4962}, volume={47(2019}, note={Gesehen am 03.01.2020}, journal={Nucleic acids research}, doi={10.1093/nar/gkz271}, } @article{UBHD-68560599, author={Krooss, Simon and Dai, Zhen and Schmidt, Florian and Rovai, Alice and Fakhiri, Julia and Dhingra, Akshay and Yuan, Qinggong and Yang, Taihua and Balakrishnan, Asha and Steinbr{\"u}ck, Lars and Srivaratharajan, Sangar and Manns, Michael Peter and Schambach, Axel and Grimm, Dirk and Bohne, Jens and Sharma, Amar Deep and B{\"u}ning, Hildegard and Ott, Michael}, title={Ex Vivo/In vivo gene editing in Hepatocytes using “all-in-one” CRISPR-adeno-associated virus vectors with a self-linearizing repair template}, year={2020}, language={eng}, issn={2589-0042}, volume={23(2020}, note={Available online 12 December 2019 ; Das PDF enth{\"a}lt zus{\"a}tzlich ein Deckblatt sowie einen Anhang ; Gesehen am 02.04.2020}, journal={iScience}, doi={10.1016/j.isci.2019.100764}, } @article{UBHD-68436873, author={Tabatabai, Julia and Fakhiri, Julia and Meyburg, Jochen and Linse, Kai-Philipp and Grimm, Dirk and Schnitzler, Paul}, title={Severe human Bocavirus 1 respiratory tract infection in an immunodeficient child with fatal outcome}, year={2019}, pages={e219-e222}, language={eng}, issn={1532-0987}, volume={38}, number={9}, note={Gesehen am 09.10.2019}, journal={The pediatric infectious disease journal}, doi={10.1097/INF.0000000000002354}, } @article{UBHD-68721825, author={Yu, Jennifer Chun and Mietzsch, Mario and Singh, Amriti and Jimenez Ybargollin, Alberto and Kailasan, Shweta and Chipman, Paul and Bhattacharya, Nilakshee and Fakhiri, Julia and Grimm, Dirk and Kapoor, Amit and Kučinskaitė-Kodzė, Indrė and Žvirblienė, Aurelija and S{\"o}derlund-Venermo, Maria and McKenna, Robert and Agbandje-McKenna, Mavis}, title={Characterization of the GBoV1 capsid and its antibody interactions}, year={2021}, pages={1-17}, language={eng}, issn={1999-4915}, volume={13}, note={Gesehen am 26.08.2021}, journal={Viruses}, doi={10.3390/v13020330}, }