@article{UBHD-69287827, author={Bjelica, Bogdan and Bartels, Maj-Britt and Hesebeck-Brinckmann, Jasper and Petri, Susanne}, title={Non-motor symptoms in patients with amyotrophic lateral sclerosis}, subtitle={current state and future directions}, year={2024}, pages={3953-3977}, language={eng}, issn={1432-1459}, volume={271}, number={7}, note={Online ver{\"o}ffentlicht: 28. Mai 2024 ; Gesehen am 08.01.2025}, journal={Journal of neurology}, doi={10.1007/s00415-024-12455-5}, } @article{UBHD-69277026, author={Meyer, Thomas and Schumann, Peggy and Weydt, Patrick and Petri, Susanne and Weishaupt, Jochen H. and Weyen, Ute and Koch, Jan C. and G{\"u}nther, René and Regensburger, Martin and Boentert, Matthias and Wiesenfarth, Maximilian and Koc, Yasemin and Kolzarek, Felix and Kettemann, Dagmar and Norden, Jenny and Bernsen, Sarah and Elmas, Zeynep and Conrad, Julian and Valkadinov, Ivan and Vidovic, Maximilian and Dorst, Johannes and Ludolph, Albert C. and Hesebeck-Brinckmann, Jasper and Spittel, Susanne and M{\"u}nch, Christoph and Maier, André and K{\"o}rtvélyessy, Péter}, title={Clinical and patient-reported outcomes and neurofilament response during tofersen treatment in SOD1-related ALS}, subtitle={a multicenter observational study over 18 months}, year={2024}, pages={333-345}, language={eng}, issn={1097-4598}, volume={70}, number={3 vom: Sept.}, note={Erstmals ver{\"o}ffentlicht: 20. Juni 2024 ; Gesehen am 26.11.2024}, journal={Muscle & nerve}, doi={10.1002/mus.28182}, } @article{UBHD-69317661, author={Wiesenfarth, Maximilian and Dorst, Johannes and Brenner, David and Elmas, Zeynep and Parlak, {\"O}zlem and Uzelac, Zeljko and Kandler, Katharina and Mayer, Kristina and Weiland, Ulrike and Herrmann, Christine and Schuster, Joachim and Freischmidt, Axel and M{\"u}ller, Kathrin and Siebert, Reiner and Bachhuber, Franziska and Simak, Tatiana and G{\"u}nther, Kornelia and Fr{\"o}hlich, Elke and Knehr, Antje and Regensburger, Martin and German, Alexander and Petri, Susanne and Grosskreutz, Julian and Klopstock, Thomas and Reilich, Peter and Sch{\"o}berl, Florian and Hagenacker, Tim and Weyen, Ute and G{\"u}nther, René and Vidovic, Maximilian and Jentsch, Martin and Haarmeier, Thomas and Weydt, Patrick and Valkadinov, Ivan and Hesebeck-Brinckmann, Jasper and Conrad, Julian and Weishaupt, Jochen H. and Schumann, Peggy and K{\"o}rtvélyessy, Peter and Meyer, Thomas and Ruf, Wolfgang Philipp and Witzel, Simon and Senel, Makbule and Tumani, Hayrettin and Ludolph, Albert Christian}, title={Effects of tofersen treatment in patients with SOD1-ALS in a “real-world” setting - a 12-month multicenter cohort study from the German early access program}, year={2024}, pages={1-12}, language={eng}, issn={2589-5370}, volume={69}, number={Artikel-ID 102495}, note={Online verf{\"u}gbar: 15. Februar 2024, Artikelversion: 15. Februar 2024 ; Gesehen am 12.03.2025}, journal={EClinicalMedicine}, doi={10.1016/j.eclinm.2024.102495}, }