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@article{UBHD-68613114, author={Garbade, Sven and Zielonka, Matthias and Mechler, Konstantin and K{\"o}lker, Stefan and Hoffmann, Georg F. and Staufner, Christian and Mengel, Eugen and Ries, Markus}, title={FDA orphan drug designations for lysosomal storage disorders}, subtitle={a cross-sectional analysis}, year={2020}, language={eng}, issn={1932-6203}, volume={15(2020}, note={Gesehen am 02.07.2020}, journal={PLOS ONE}, doi={10.1371/journal.pone.0230898}, }