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@incollection{UBHD-68910579, author={Garbade, Sven and Zielonka, Matthias and Mechler, Konstantin and K{\"o}lker, Stefan and Hoffmann, Georg F. and Staufner, Christian and Mengel, Eugen and Ries, Markus}, title={FDA orphan drug designations for lysosomal storage disorders}, subtitle={a cross sectional analysis}, year={2020}, pages={1-29}, language={eng}, note={Gesehen am 25.04.2022}, booktitle={medRxiv}, doi={10.1101/2020.01.05.20016568}, }