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TY - `JOUR` AU - Pan, Yi AU - Shen, Nan AU - Jung-Klawitter, Sabine AU - Betzen, Christian AU - Hoffmann, Georg F. AU - Blau, Nenad TI - CRISPR RNA-guided FokI nucleases repair a PAH variant in a phenylketonuria model PY - 2016 LA - eng SP - 7 S. T2 - Scientific reports PY - 2016 VL - 6(2016) Article number: 35794 SI - 7 Seiten DO - 10.1038/srep35794 AN - UBHD-68210743 ER -