
Schmidt, Manfred Dr. sc. hum.Universität HeidelbergHeidelberg
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- Ruggiero, Eliana (9)
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Publications in heiBIB 
- Suleman, Saqlain: HIV- 1 lentivirus tethering to the genome is associated with transcription factor binding sites found in genes that favour virus survival / Saqlain Suleman, Annette Payne, Johnathan Bowden, Sharmin Al Haque, Marco Zahn, Serena Fawaz, Mohamm… , 5 May 2022. - 10 S.
In: Gene therapy, ISSN 1476-5462. 29(2022), 12, Seite 720-729
DOI: 10.1038/s41434-022-00335-4
- Hanna, Bola: Interleukin-10 receptor signaling promotes the maintenance of a PD-1int TCF-1+ CD8+ T cell population that sustains anti-tumor immunity / Bola S. Hanna, Laura Llaó-Cid, Murat Iskar, Philipp M. Roessner, Lara C. Klett, John K. L. Wong, Yas… , December 14, 2021. - 28 S.
In: Immunity, ISSN 1097-4180. 54(2021), 12, Seite 2825-2841
DOI: 10.1016/j.immuni.2021.11.004
- Kohn, Donald B.: Autologous ex vivo lentiviral gene therapy for adenosine deaminase deficiency / D.B. Kohn, C. Both, K.L. Shaw, J. Xu-Bayford, E. Garabedian, V. Trevisan, D.A. Carbonaro-Sarracino, … , May 11, 2021. - 12 S.
In: The New England journal of medicine, ISSN 1533-4406. 384(2021), 21 vom: Mai, Seite 2002-2013
DOI: 10.1056/NEJMoa2027675
- Herbst, Friederike: The balance between the intronic miR-342 and its host gene Evl determines hematopoietic cell fate decision / Friederike Herbst, Tonio J.L. Lang, Elias S.P. Eckert, Peer Wünsche, Alexander A. Wurm, Tim Kindinge… , 21 May 2021. - 16 S.
In: Leukemia, ISSN 1476-5551. 35(2021), 10, Seite 2948-2963
DOI: 10.1038/s41375-021-01267-5
- Xydia, Maria: Common clonal origin of conventional T cells and induced regulatory T cells in breast cancer patients / Maria Xydia, Raheleh Rahbari, Eliana Ruggiero, Iain Macaulay, Maxime Tarabichi, Robert Lohmayer, Ste… , 18 February 2021. - 18 S.
In: Nature Communications, ISSN 2041-1723. 12(2021), Artikel-ID 1119, Seite 1-18
DOI: 10.1038/s41467-021-21297-y
- Schenkwein, Diana: Efficient nuclease-directed integration of lentivirus vectors into the human ribosomal DNA locus / Diana Schenkwein, Saira Afzal, Alisa Nousiainen, Manfred Schmidt, Seppo Ylä-Herttuala, 23 May 2020. - 18 S.
In: Molecular therapy, ISSN 1525-0024. 28(2020), 8, Seite 1858-1875
DOI: 10.1016/j.ymthe.2020.05.019
- Darche, Fabrice Fernand: Pacemaker cell characteristics of differentiated and HCN4-transduced human mesenchymal stem cells / Fabrice F. Darche, Rasmus Rivinius, Eva Köllensperger, Uwe Leimer, Günter Germann, Anja Seckinger, D… , 07 July 2019. - 16 S.
In: Life sciences, ISSN 1879-0631. 232(2019), Artikel-ID 116620, Seite 1-16
DOI: 10.1016/j.lfs.2019.116620
- Rio, Paula: Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia / Paula Río, Susana Navarro, Wei Wang, Rebeca Sánchez-Domínguez, Roser M. Pujol, José C. Segovia, Mass… , 09 September 2019. - 6 S.
In: Nature medicine, ISSN 1546-170X. 25(2019), 9, Seite 1396-1401
DOI: 10.1038/s41591-019-0550-z
- Shangaris, Panicos: In utero gene therapy (IUGT) using GLOBE lentiviral vector phenotypically corrects the heterozygous humanised mouse model and its progress can be monitored using MRI techniques / Panicos Shangaris, Stavros P. Loukogeorgakis, Sindhu Subramaniam, Christina Flouri, Laurence H. Jack… , 12 August 2019. - 17 S.
In: Scientific reports, ISSN 2045-2322. 9(2019), Artikel-ID 11592, Seite 1-17
DOI: 10.1038/s41598-019-48078-4
- Lucic, Bojana: Spatially clustered loci with multiple enhancers are frequent targets of HIV-1 integration / Bojana Lucic, Heng-Chang Chen, Maja Kuzman, Eduard Zorita, Julia Wegner, Vera Minneker, Wei Wang, Ra… , 06 September 2019. - 12 S.
In: Nature Communications, ISSN 2041-1723. 10(2019) Artikel-Nummer 4059, 12 Seiten
DOI: 10.1038/s41467-019-12046-3
- Chan, Jerry K. Y.: Therapeutic expression of human clotting factors IX and X following adeno-associated viral vector-mediated intrauterine gene transfer in early-gestation fetal macaques / Jerry K.Y. Chan, Irene Gil-Farina, Nuryanti Johana, Cecilia Rosales, Yi Wan Tan, Jessika Ceiler, Jen… , 27 Feb 2019. - 14 S.
In: The FASEB journal, ISSN 1530-6860. 33(2019), 3, Seite 3954-3967
DOI: 10.1096/fj.201801391R
- Afzal, Saira: Systematic comparative study of computational methods for T-cell receptor sequencing data analysis / Saira Afzal, Irene Gil-Farina, Richard Gabriel, Shahzad Ahmad, Christof von Kalle, Manfred Schmidt a… , 2019. - 13 S.
In: Briefings in bioinformatics, ISSN 1477-4054. 20(2019), 1, Seite 222-234
DOI: 10.1093/bib/bbx111
- Senís Herrero, Elena: AAV vector-mediated in vivo reprogramming into pluripotency / Elena Senís, Lluc Mosteiro, Stefan Wilkening, Ellen Wiedtke, Ali Nowrouzi, Saira Afzal, Raffaele Fro… , 09 July 2018. - 14 S.
In: Nature Communications, ISSN 2041-1723. 9(2018) Article number: 2651, 14 Seiten
DOI: 10.1038/s41467-018-05059-x
- Hanna, Bola S.: Control of chronic lymphocytic leukemia development by clonally-expanded CD8 + T-cells that undergo functional exhaustion in secondary lymphoid tissues / Bola S. Hanna, Philipp M. Roessner, Haniyeh Yazdanparast, Dolors Colomer, Elias Campo, Sabrina Kugle… , 2019. - 13 S.
In: Leukemia, ISSN 1476-5551. 33(2019), 3, Seite 625-637
DOI: 10.1038/s41375-018-0250-6
- Wünsche, Peer: Mapping active gene-regulatory regions in human repopulating long-term HSCs / Peer Wünsche, Elias S.P. Eckert, Tim Holland-Letz, Anna Paruzynski, Agnes Hotz-Wagenblatt, Raffaele … , 5 July 2018. - 15 S.
In: Cell stem cell, ISSN 1875-9777. 23(2018), 1, Seite 132-146
DOI: 10.1016/j.stem.2018.06.003
- Wang, Wei: The clonal fate of live cells / Wei Wang, Raffaele Fronza, Manfred Schmidt, 16 June 2017. - 3 S.
In: Molecular therapy, ISSN 2329-0501. 5(2017), Seite 93-95
DOI: 10.1016/j.omtm.2017.03.007
- Ball, Claudia R.: Succession of transiently active tumor‐initiating cell clones in human pancreatic cancer xenografts / Claudia R Ball, Felix Oppel, Karl Roland Ehrenberg, Taronish D Dubash, Sebastian M Dieter, Christoph… , 19 May 2017. - 15 S.
In: EMBO molecular medicine, ISSN 1757-4684. 9(2017), 7, Seite 918-932
DOI: 10.15252/emmm.201607354
- Dieter, Sebastian M.: Patient-derived xenografts of gastrointestinal cancers are susceptible to rapid and delayed B-lymphoproliferation / Sebastian M. Dieter, Klara M. Giessler, Mark Kriegsmann, Taronish D. Dubash, Lino Möhrmann, Erik R. … , 2017. - 8 S.
In: International journal of cancer, ISSN 1097-0215. 140(2017), 6, Seite 1356-1363
DOI: 10.1002/ijc.30561
- Knipping, Friederike: Genome-wide specificity of highly efficient TALENs and CRISPR/Cas9 for T cell receptor modification / Friederike Knipping, Mark J. Osborn, Karl Petri, Jakub Tolar, Hanno Glimm, Christof von Kalle, Manfr… , 12 February 2017. - 12 S.
In: Molecular therapy, ISSN 2329-0501. 4(2017), Seite 213-224
DOI: 10.1016/j.omtm.2017.01.005
- Afzal, Saira: GENE-IS : time-efficient and accurate analysis of viral integration events in large-scale gene therapy data / Saira Afzal, Stefan Wilkening, Christof von Kalle, Manfred Schmidt, and Raffaele Fronza, 2017. - 7 S.
In: Molecular therapy, ISSN 2162-2531. 6(2017), Seite 133-139
DOI: 10.1016/j.omtn.2016.12.001
- Scholz, Simone: Lentiviral vector promoter is decisive for aberrant transcript formation / Simone J. Scholz, Raffaele Fronza, Cynthia C. Bartholomä, Daniela Cesana, Eugenio Montini, Christof … , August 18, 2017. - 11 S.
In: Human gene therapy, ISSN 1557-7422. 28(2017), 10, Seite 875-885
DOI: 10.1089/hum.2017.162
- Gießler, Klara Monika: Genetic subclone architecture of tumor clone-initiating cells in colorectal cancer / Klara M. Giessler, Kortine Kleinheinz, Daniel Huebschmann, Gnana Prakash Balasubramanian, Taronish D… , 2017. - 16 S.
In: Journal of experimental medicine, ISSN 1540-9538. 214(2017), 7, Seite 2073-2088
DOI: 10.1084/jem.20162017
- Mattar, Citra Nurfarah Zaini: In utero transfer of adeno-associated viral vectors produces long-term factor IX levels in a cynomolgus macaque model / Citra N. Z. Mattar, Irene Gil-Farina, Cecilia Rosales, Nuryanti Johana, Yvonne Yi Wan Tan, Jenny McI… , 2017. - 11 S.
In: Molecular therapy, ISSN 1525-0024. 25(2017), 8, Seite 1843-1853
DOI: 10.1016/j.ymthe.2017.04.003
- Gonzaléz-Prieto, Coral: The conjugative relaxase TrwC promotes integration of foreign DNA in the human genome / Coral González-Prieto, Richard Gabriel, Christoph Dehio, Manfred Schmidt, Matxalen Llosa, 2017. - 16 S.
In: Applied and environmental microbiology, ISSN 1098-5336. 83(2017,12) Artikel-Nummer e00207-17, 16 Seiten
DOI: 10.1128/AEM.00207-17
- Schmidt, Manfred: Reply to “Wild-type AAV insertions in hepatocellular carcinoma do not inform debate over genotoxicity risk of vectorized AAV” / Manfred Schmidt, Irene Gil-Farina and Hildegard Büning, 14 December 2016. - 2 S.
In: Molecular therapy, ISSN 1525-0024. 24(2016), 4, Seite 661-662
DOI: 10.1038/mt.2016.48
- Dubash, Taronish Dorab: Phenotypic differentiation does not affect tumorigenicity of primary human colon cancer initiating cells / Taronish D. Dubash, Christopher M. Hoffmann, Felix Oppel, Klara M. Giessler, Sarah Weber, Sebastian … , 2016. - 8 S.
In: Cancer letters, ISSN 1872-7980. 371(2016), 2, Seite 326-333
DOI: 10.1016/j.canlet.2015.11.037
- Osborn, Mark J.: Evaluation of TCR gene editing achieved by TALENs, CRISPR/Cas9, and megaTAL nucleases / Mark J Osborn, Beau R Webber, Friederike Knipping, Cara-lin Lonetree, Nicole Tennis, Anthony P DeFeo… , 5 January 2016. - 12 S.
In: Molecular therapy, ISSN 1525-0024. 24(2016), 3, Seite 570-581
DOI: 10.1038/mt.2015.197
- Gil-Fariña, Irene: Recombinant AAV integration is not associated with hepatic genotoxicity in nonhuman primates and patients / Irene Gil-Farina, Raffaele Fronza, Christine Kaeppel, Esperanza Lopez-Franco, Valerie Ferreira, Deli… , 5 April 2016. - 6 S.
In: Molecular therapy, ISSN 1525-0024. 24(2016), 6, Seite 1100-1105
DOI: 10.1038/mt.2016.52
- D'Avola, Delia: Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria / Delia D’Avola, Esperanza López-Franco, Bruno Sangro, Astrid Pañeda, Nadina Grossios, Irene Gil-Farin… , 17 May 2016. - 8 S.
In: Journal of hepatology, ISSN 1600-0641. 65(2016), 4, Seite 776-783
DOI: 10.1016/j.jhep.2016.05.012
- Gil-Fariña, Irene: Interaction of vectors and parental viruses with the host genome / Irene Gil-Farina, Manfred Schmidt, 28 July 2016. - 6 S.
In: Current opinion in virology, ISSN 1879-6265. 21(2016), Supplement C, Seite 35-40
DOI: 10.1016/j.coviro.2016.07.004
- Giordano, Frank Anton: High-throughput monitoring of integration site clonality in preclinical and clinical gene therapy studies / Frank A. Giordano, Jens-Uwe Appelt, Barbara Link, Sebastian Gerdes, Christina Lehrer, Simone Scholz,… , 2015. - 8 S.
In: Molecular therapy, ISSN 2329-0501. 2(2015), Artikel-ID 14061, Seite 1-8
DOI: 10.1038/mtm.2014.61
- Negre, Olivier: Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease / Olivier Negre, Cynthia Bartholomae, Yves Beuzard, Marina Cavazzana, Lauryn Christiansen, Céline Cour… , 2015 Feb.. - 18 S.
In: Current gene therapy, ISSN 1875-5631. 15(2015), 1, Seite 64-81
DOI: 10.2174/1566523214666141127095336
- Siler, Ulrich: Successful combination of sequential gene therapy and rescue Allo-HSCT in two children with X-CGD$iImportance of timing / Ulrich Siler, Anna Paruzynski, Heidi Holtgreve-Grez, Elena Kuzmenko, Ulrike Koehl, Eleonore D. Renne… , 2015. - 12 S.
In: Current gene therapy, ISSN 1875-5631. 15(2015), 4, Seite 416-427
DOI: 10.2174/1566523215666150515145255
- Fronza, Raffaele: A graph based framework to model virus integration sites / Raffaele Fronza, Alessandro Vasciaveo, Alfredo Benso, Manfred Schmidt, 2016. - 9 S.
In: Computational and structural biotechnology journal, ISSN 2001-0370. 14(2016), Seite 69-77
DOI: 10.1016/j.csbj.2015.10.006
- Cantore, Alessio: Liver-directed lentiviral gene therapy in a dog model of hemophilia B / Alessio Cantore, Marco Ranzani, Cynthia C. Bartholomae, Monica Volpin, Patrizia Della Valle, Frances… , 4 March 2015. - 12 S.
In: Science translational medicine, ISSN 1946-6242. 7(2015,227) Artikel-Nummer 277ra28, 12 Seiten
DOI: 10.1126/scitranslmed.aaa1405
- Papanikolaou, Eleni: Cell cycle status of CD34+ hemopoietic stem cells determines lentiviral integration in actively transcribed and development-related genes / Eleni Papanikolaou, Anna Paruzynski, Ioannis Kasampalidis, Annette Deichmann, Evangelos Stamateris, … , 10 February 2015. - 14 S.
In: Molecular therapy, ISSN 1525-0024. 23(2015), 4, Seite 683-696
DOI: 10.1038/mt.2014.246
- Gardyan, Adriane: Identification of NY-BR-1-specific CD4+ T cell epitopes using HLA-transgenic mice / Adriane Gardyan, Wolfram Osen, Inka Zörnig, Lilli Podola, Maria Agarwal, Sebastian Aulmann, Eliana R… , 12 Nov 2014. - 10 S.
In: International journal of Cancer Studies & Research, ISSN 2167-9118. 136(2015), 11, Seite 2588-2597
DOI: 10.1002/ijc.29322
- Gabriel, Richard: Mapping the precision of genome editing / Richard Gabriel, Christof von Kalle and Manfred Schmidt, 06 February 2015. - 3 S.
In: Nature biotechnology, ISSN 1546-1696. 33(2015), 2, Seite 150-152
DOI: 10.1038/nbt.3142
- Bergot, Anne-Sophie: TCR sequences and tissue distribution discriminate the subsets of naïve and activated/memory Treg cells in mice / Anne-Sophie Bergot, Wahiba Chaara, Eliana Ruggiero, Encarnita Mariotti-Ferrandiz, Sophie Dulauroy, M… , 27 February 2015. - 11 S.
In: European journal of immunology, ISSN 1521-4141. 45(2015), 5, Seite 1524-1534
DOI: 10.1002/eji.201445269
- Petri, Karl: Presence of a trs-like motif promotes rep-mediated wild-type adeno-associated virus type 2 integration / Karl Petri, Richard Gabriel, Leticia Agundez, Raffaele Fronza, Saira Afzal, Christine Kaeppel, R. Mi… , July 2015. - 5 S.
In: Journal of virology, ISSN 1098-5514. 89(2015), 14, Seite 7428-7432
DOI: 10.1128/JVI.00426-15
- Molina-Estévez, Francisco Javier: Lentiviral-mediated gene therapy in fanconi anemia-a mice reveals long-term engraftment and continuous turnover of corrected HSCs / F. Javier Molina-Estevez, Ali Nowrouzi, MLuz L. Lozano, Anne Galy, Sabine Charrier, Christof von Kal… , 1 December 2015. - 13 S.
In: Current gene therapy, ISSN 1875-5631. 15(2015), 6, Seite 550-562
DOI: 10.2174/1566523215666150929110903
- Sundarasetty, Bala Sai: Generation of lentivirus-induced dendritic cells under GMP-compliant conditions for adaptive immune reconstitution against cytomegalovirus after stem cell transplantation / Bala Sai Sundarasetty, Stephan Kloess, Olaf Oberschmidt, Sonja Naundorf, Klaus Kuehlcke, Anusara Dae… , 22 July 2015. - 19 S.
In: Journal of translational medicine, ISSN 1479-5876. 13(2015) Artikel-Nummer 240, 19 Seiten
DOI: 10.1186/s12967-015-0599-5
- Alaee, Farhang: Biodistribution of LV-TSTA transduced rat bone marrow cells used for “ex-vivo” regional gene therapy for bone repair / Farhang Alaee, Cynthia Bartholomae, Osamu Sugiyama, Mandeep S. Virk, Hicham Drissi, Qian Wu, Manfred… , 2015. - 11 S.
In: Current gene therapy, ISSN 1875-5631. 15(2015), 5, Seite 481-491
DOI: 10.2174/1566523215666150812120229
- Richards, David: The contained self-reactive peripheral T cell repertoire : size, diversity, and cellular composition / David M. Richards, Eliana Ruggiero, Ann-Cathrin Hofer, Julian P. Sefrin, Manfred Schmidt, Christof v… , September 2015. - 13 S.
In: The journal of immunology, ISSN 1550-6606. 195(2015), 5, Seite 2067-2079
DOI: 10.4049/jimmunol.1500880
- Siler, Ulrich: Successful combination of cequential gene therapy and rescue allo-HSCT in two children with X-CGD : importance of timing / Ulrich Siler, Anna Paruzynski, Heidi Holtgreve-Grez, Elena Kuzmenko, Ulrike Koehl, Eleonore D. Renne… , 2015. - 12 S.
In: Current gene therapy, ISSN 1875-5631. 15(2015), 4, Seite 416-427
DOI: 10.2174/1566523215666150515145255
- Sundarasetty, Bala Sai: Lentivirus-induced ‘Smart’ dendritic cells : pharmacodynamics and GMP-compliant production for immunotherapy against TRP2-positive melanoma / B.S. Sundarasetty, L. Chan, D. Darling, G. Giunti, F. Farzaneh, F. Schenck, S. Naundorf, K. Kuehlcke… , September 2015. - 14 S.
In: Gene therapy, ISSN 1476-5462. 22(2015), 9, Seite 707-720
DOI: 10.1038/gt.2015.43
- Ruggiero, Eliana: High-resolution analysis of the human T-cell receptor repertoire / Eliana Ruggiero, Jan P. Nicolay, Raffaele Fronza, Anne Arens, Anna Paruzynski, Ali Nowrouzi, Gökçe Ü… , 1 September 2015
In: Nature Communications, ISSN 2041-1723. 6(2015) Artikel-Nummer 8081, 7 Seiten
DOI: 10.1038/ncomms9081
- Negre, Olivier: Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease / Olivier Negre, Cynthia Bartholomä, Yves Beuzard, Marina Cavazzana, Lauryn Christiansen, Céline Courn… , 2015. - 18 S.
In: Current gene therapy, ISSN 1875-5631. 15(2015), 1, Seite 64-81
DOI: 10.2174/1566523214666141127095336
- Büning, Hildegard: Adeno-associated vector toxicity : to be or not to be? / Hildegard Büning and Manfred Schmidt, November 2015. - 3 S.
In: Molecular therapy, ISSN 1525-0024. 23(2015), 11, Seite 1673-1675
DOI: 10.1038/mt.2015.182
- Oliveira, Giacomo: Erratum for the Research Article: Tracking genetically engineered lymphocytes long-term reveals the dynamics of T cell immunological memory / G. Oliveira, E. Ruggiero, M.T.L. Stanghellini, N. Cieri, M. D’Agostino, R. Fronza, C. Lulay, F. Dion… , 23 December 2015
In: Science translational medicine, ISSN 1946-6242. 7(2015,319) Artikel-Nummer 319er9, 1 Seite
DOI: 10.1126/scitranslmed.aaf1040
- Oliveira, Giacomo: Tracking genetically engineered lymphocytes long-term reveals the dynamics of T cell immunological memory / Giacomo Oliveira, Eliana Ruggiero, Maria Teresa Lupo Stanghellini, Nicoletta Cieri, Mattia D’Agostin… , 9 December 2015
In: Science translational medicine, ISSN 1946-6242. 7(2015,317) Artikel-Nummer 317ra198, 14 Seiten
DOI: 10.1126/scitranslmed.aac8265
- Osborn, Mark J.: Fanconi anemia gene editing by the CRISPR/Cas9 system / Mark J. Osborn, Richard Gabriel, Beau R. Webber, Anthony P. DeFeo, Amber N. McElroy, Jordan Jarjour,… , December 3, 2014. - 13 S.
In: Human gene therapy, ISSN 1557-7422. 26(2014), 2, Seite 114-126
DOI: 10.1089/hum.2014.111
- Schönfeld, Kurt: Selective inhibition of tumor growth by clonal NK cells expressing an ErbB2/HER2-specific chimeric antigen receptor / Kurt Schönfeld, Christiane Sahm, Congcong Zhang, Sonja Naundorf, Christian Brendel, Marcus Odendahl,… , 2015. - 9 S.
In: Molecular therapy, ISSN 1525-0024. 23(2015), 2, Seite 330-338
DOI: 10.1038/mt.2014.219
- Käppel, Christine: Reply to: NGS library preparation may generate artifactual integration sites of AAV vectors / Christine Kaeppel, Stuart G Beattie, Raffaele Fronza, Richard van Logtenstein, Florence Salmon, Sabi… , 05 June 2014. - 578-579$t2
In: Nature medicine, ISSN 1546-170X. 20(2014), 6
DOI: 10.1038/nm.3584
- Bartholomä, Cynthia C.: Integration-deficient lentiviral vectors expressing codon-optimized R338L human FIX restore normal hemostasis in hemophilia B mice / Thipparat Suwanmanee, Genlin Hu, Tong Gui, Cynthia C Bartholomae, Ina Kutschera, Christof von Kalle,… , 7 January 2014. - 8 S.
In: Molecular therapy, ISSN 1525-0024. 22(2014), 3, Seite 567-574
DOI: 10.1038/mt.2013.188
- Kalle, Christof von: Vector integration and tumorigenesis / Christof von Kalle, Annette Deichmann and Manfred Schmidt, June 2014. - 7 S.
In: Human gene therapy, ISSN 1557-7422. 25(2014), 6, Seite 475-481
DOI: 10.1089/hum.2014.2525
- Gabriel, Richard: Linear amplification mediated PCR : localization of genetic elements and characterization of unknown flanking DNA / Richard Gabriel, Ina Kutschera, Cynthia C. Bartholomae, Christof von Kalle, Manfred Schmidt, 25 June 2014. - 1 Online-Ressource (1 Videodatei, 11:57 min) : farbig
In: JoVE, ISSN 1940-087X. (2014,88) Artikel-Nummer e51543, 8 Seiten
DOI: 10.3791/51543
- Petri, Karl: Comparative next-generation sequencing of adeno-associated virus inverted terminal repeats / Karl Petri, Raffaele Fronza, Richard Gabriel, Christine Käppel, Ali Nowrouzi, R. Michael Linden, Els… , May 2014. - 5 S.
In: BioTechniques, ISSN 1940-9818. 56(2014), 5, Seite 269-273
DOI: 10.2144/000114170
- Stephan, Christoph: Impact of raltegravir on HIV-1 RNA and DNA forms following initiation of antiretroviral therapy in treatment-naive patients / Christoph Stephan, Hanna-Mari Baldauf, Joanne Barry,Frank A. Giordano, Cynthia C. Bartholomae, Annet… , 2014. - 10 S.
In: The journal of antimicrobial chemotherapy, ISSN 1460-2091. 69(2014), 10, Seite 2809-2818
DOI: 10.1093/jac/dku213
- Cesana, Daniela: Uncovering and dissecting the genotoxicity of self-inactivating lentiviral vectors in vivo / Daniela Cesana, Marco Ranzani, Monica Volpin, Cynthia Bartholomae, Caroline Duros, Alexandre Artus, … , 2014. - 12 S.
In: Molecular therapy, ISSN 1525-0024. 22(2014), 4, Seite 774-785
DOI: 10.1038/mt.2014.3
- Saeed, Muhammad: Comparison between several integrase-defective lentiviral vectors reveals increased integration of an HIV vector bearing a D167H mutant / Muhammad Qamar Saeed, Noelle Dufour, Cynthia Bartholmae, Urzula Sieranska, Malaika Knopf, Eloïse Thi… , 2014. - 12 S.
In: Molecular therapy, ISSN 2162-2531. 3(2014) Artikel-Nr.e213,12S
DOI: 10.1038/mtna.2014.65
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